Current Research Studies

Expanded Access Protocol of Apitegromab for Patients With Spinal Muscular Atrophy

Apitegromab EAP

Condition(s): Diseases Of The Nervous System
Phase: N/A
Clinicaltrials.gov ID: NCT05156320

What is the goal of the study?

Provide apitegromab to patients prior to FDA approval.

Who can participate in the study?

Non-ambulatory patients 2 years or older with Spinal Muscular Atrophy

Study Team:

PI (Study Doctor): Seth Perlman
Study Team Member: Janaki O’Brien, [email protected]