Current Research Studies
A Long-term Multicenter Prospective Observational Study Evaluating the Comparative Effectiveness and Safety of Sarepta Gene Transfer Therapy vs. Standard of Care in Participants with Duchenne Muscular Dystrophy under Conditions of Routine Clinical Practice
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What is the goal of the study?
This is a drug study phase 4 Observational Study Evaluating the Comparative Effectiveness and Safety of Sarepta Gene Transfer Therapy (delandistrogene moxeparvovec-rokl) vs. Standard of Care.
Who can participate in the study?
Please contact the study team listed below to learn more.