Current Research Studies

Mucopolysccharidosis VII Disease Monitoring Program (MPS VII DMP)

MPSVII_DMP

Phase: IV
Clinicaltrials.gov ID: NCT03604835

What is the goal of the study?

The aim of this study is to collect data on patients with MPS VII to provide a comprehensive dataset on the clinical presentation, heterogeneity, and disease progression, as well as meaningful standardized ICH GCP-quality data collected in-clinic across multiple sites globally.

Who can participate in the study?

Please contact the study team listed below to learn more.

Study Team:

PI (Study Doctor): Terry Kho
Study Team Member: Hayden Vreugdenhil, [email protected]