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Current Research Studies

Mucopolysccharidosis VII Disease Monitoring Program (MPS VII DMP)

MPSVII_DMP

Phase: IV
Clinicaltrials.gov ID: NCT03604835

What is the goal of the study?

The aim of this study is to collect data on patients with MPS VII to provide a comprehensive dataset on the clinical presentation, heterogeneity, and disease progression, as well as meaningful standardized ICH GCP-quality data collected in-clinic across multiple sites globally.

Who can participate in the study?

Please contact the study team listed below to learn more.

Study Team:

PI (Study Doctor): Emily Shelkowitz
Study Team Member: Hayden Vreugdenhil, [email protected]

Seattle Children’s complies with applicable federal and other civil rights laws and does not discriminate, exclude people or treat them differently based on race, color, religion (creed), sex, gender identity or expression, sexual orientation, national origin (ancestry), age, disability, or any other status protected by applicable federal, state or local law. Financial assistance for medically necessary services is based on family income and hospital resources and is provided to children under age 21 whose primary residence is in Washington, Alaska, Montana or Idaho.