Current Research Studies

Long-Chain Fatty Acid Oxidation Disorders In-Clinic Disease Monitoring Program (LC-FAOD DMP)

UX007-CL401

  • Condition(s): Other
  • Phase: Post-Approval/Marketing
  • Clinicaltrials.gov ID: NCT04632953

What is the goal of the study?

The purpose of this study is to investigate the long-term safety and effectiveness of triheptanoin in adults and pediatric patients with LC-FAOD and to assess pregnancy and maternal complications in all patients with LC-FAOD, and adverse effects on the developing fetus, neonate, and infant.

Who can participate in the study?

Please contact the study team listed below to learn more.

Study Team: