Cerliponase alfa Observation Study
Cerliponase Alfa Observational Study
What is the goal of the study?
This is a multicenter observational study for patients with a confirmed diagnosis of neuronal ceroid lipofuscinosis type 2 (CLN2 disease), also known as TPP1 deficiency, who intend to be or are currently being treated with cerliponase alfa. The primary objective of the study is to evaluate long-term safety of cerliponase alfa in patient with CLN2 disease.
Who can participate in the study?
Please contact the study team listed below to learn more.