Current Research Studies

An Open-Label, Multicenter, Extension Trial to Evaluate the Long-Term Safety and Efficacy of Apitegromab in Patients with Type 2 and Type 3 Spinal Muscular Atrophy Who Completed Previous Investigational Trials of Apitegromab


What is the goal of the study?

This is the open-label extension protocol for STUDY00003845 (SMA_SRK_003_Sapphire).

Who can participate in the study?

Please contact the study team listed below to learn more.

Study Team: