Current Research Studies
A Prospective, Observational Study Evaluating the Real-World Experience of Givinostat in Patients with Duchenne Muscular Dystrophy
Givinostat Registry
What is the goal of the study?
Is an observational study, that evaluate the experience of Givinostat (DUVYZAT®). Givinostat is the first non-steroidal treatment for use in patients with DMD irrespective of the specific genetic variant. It is an orally available histone deacetylase inhibitor indicated for treatment of DMD in patients aged 6 years and older. The Food and Drug Administration (FDA) approved it in March 2024.
Who can participate in the study?
Please contact the study team listed below to learn more.