A Long-term Follow-up Study of Patients in LogicBio Clinical Trials for Methylmalonic Acidemia Characterized by MMUT Mutations Who Received hLB-001
What is the goal of the study?
This is a non-interventional long-term follow-up study of patients who have participated in LogicBio studies for the treatment of MMA and received hLB-001. Patients will rollover from the treatment study into this long-term follow-up study for continuous safety monitoring, as well as monitoring of continued efficacy and durability of response. Patients will be followed for a period of 15 years which includes the duration of time that the patient was in the treatment study.
Who can participate in the study?
Please contact the study team listed below to learn more.