$125k a Dose? Price of Game-Changing Drug for Kids Frustrates Seattle Doctor

$125k a Dose? Price of Game-Changing Drug for Kids Frustrates Seattle Doctor

After 20 years of treating people with spinal muscular atrophy (SMA), Dr. Susan Apkon believes she finally has a treatment that can change her patients’ lives. She’s talking about a new drug called Spinraza, which the FDA approved in December. At Seattle Children’s Hospital, Apkon has already started treatment on around 25 kids with SMA, a genetic disorder that affects the nervous system and robs patients of their muscle control and strength.

About Seattle Children’s

Seattle Children’s mission is to provide hope, care and cures to help every child live the healthiest and most fulfilling life possible. Together, Seattle Children’s Hospital, Research Institute and Foundation deliver superior patient care, identify new discoveries and treatments through pediatric research, and raise funds to create better futures for patients.

Ranked as one of the top children’s hospitals in the country by U.S. News & World Report, Seattle Children’s serves as the pediatric and adolescent academic medical center for Washington, Alaska, Montana and Idaho – the largest region of any children’s hospital in the country. As one of the nation’s top five pediatric research centers, Seattle Children’s Research Institute is internationally recognized for its work in neurosciences, immunology, cancer, infectious disease, injury prevention and much more. Seattle Children’s Hospital and Research Foundation works with the Seattle Children’s Guild Association, the largest all-volunteer fundraising network for any hospital in the country, to gather community support and raise funds for uncompensated care and research. Join Seattle Children’s bold initiative – It Starts With Yes: The Campaign for Seattle Children’s – to transform children’s health for generations to come.

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