FDA clears drug for leading form of cystic fibrosis
Source: The Seattle Times
Federal health officials have approved a new combination drug for the most common form of cystic fibrosis, the debilitating inherited disease that causes internal mucus buildup, lung infections and early death. But it will come at a steep price — more than $250,000 for a year’s treatment. Two large Phase 3 clinical trials confirming the drug’s effectiveness were co-led by Dr. Bonnie Ramsey, a professor of pediatrics at the University of Washington School of Medicine and the Center for Clinical and Translational Research at Seattle Children’s Research Institute. About 25 Washington state patients participated in the trials.
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